| Transplantation of genetically corrected human iPSC-derived progenitors in mice with limb-girdle muscular dystrophy FS Tedesco, MFM Gerli, L Perani, S Benedetti, F Ungaro, M Cassano, ... Science translational medicine 4 (140), 140ra89-140ra89, 2012 | 320 | 2012 |
| Stem cell–mediated transfer of a human artificial chromosome ameliorates muscular dystrophy FS Tedesco, H Hoshiya, G D’Antona, MFM Gerli, G Messina, S Antonini, ... Science translational medicine 3 (96), 96ra78-96ra78, 2011 | 183 | 2011 |
| Intra‐arterial transplantation of HLA‐matched donor mesoangioblasts in Duchenne muscular dystrophy G Cossu, SC Previtali, S Napolitano, MP Cicalese, FS Tedesco, ... EMBO molecular medicine 7 (12), 1513-1528, 2015 | 173 | 2015 |
| Efficient derivation and inducible differentiation of expandable skeletal myogenic cells from human ES and patient-specific iPS cells SM Maffioletti, MFM Gerli, M Ragazzi, S Dastidar, S Benedetti, ... Nature Protocols 10 (7), 941-958, 2015 | 106 | 2015 |
| In vivo generation of a mature and functional artificial skeletal muscle C Fuoco, R Rizzi, A Biondo, E Longa, A Mascaro, K Shapira‐Schweitzer, ... EMBO molecular medicine 7 (4), 411-422, 2015 | 87 | 2015 |
| Embryonic Stem Cell–Derived CD166+ Precursors Develop Into Fully Functional Sinoatrial-Like Cells A Scavone, D Capilupo, N Mazzocchi, A Crespi, S Zoia, G Campostrini, ... Circulation research 113 (4), 389-398, 2013 | 82 | 2013 |
| Repair or replace? Exploiting novel gene and cell therapy strategies for muscular dystrophies S Benedetti, H Hoshiya, FS Tedesco The FEBS journal 280 (17), 4263-4280, 2013 | 76 | 2013 |
| PW1/Peg3 expression regulates key properties that determine mesoangioblast stem cell competence C Bonfanti, G Rossi, FS Tedesco, M Giannotta, S Benedetti, R Tonlorenzi, ... Nature communications 6 (1), 1-13, 2015 | 70 | 2015 |
| Dll4 and PDGF-BB convert committed skeletal myoblasts to pericytes without erasing their myogenic memory O Cappellari, S Benedetti, A Innocenzi, FS Tedesco, A Moreno-Fortuny, ... Developmental cell 24 (6), 586-599, 2013 | 69 | 2013 |
| Vascular growth factors play critical roles in kidney glomeruli. L Gnudi, S Benedetti, AS Woolf, DA Long Clinical Science 129 (12), 1225-36, 2015 | 60 | 2015 |
| Combined Notch and PDGF signaling enhances migration and expression of stem cell markers while inducing perivascular cell features in muscle satellite cells MFM Gerli, LA Moyle, S Benedetti, G Ferrari, E Ucuncu, M Ragazzi, ... Stem cell reports 12 (3), 461-473, 2019 | 46 | 2019 |
| Targeting endothelial junctional adhesion molecule‐A/EPAC/Rap‐1 axis as a novel strategy to increase stem cell engraftment in dystrophic muscles M Giannotta, S Benedetti, FS Tedesco, M Corada, M Trani, R D'Antuono, ... EMBO molecular medicine, e201302520, 2014 | 44 | 2014 |
| Reversible immortalisation enables genetic correction of human muscle progenitors and engineering of next-generation human artificial chromosomes for Duchenne muscular dystrophy. BS Uno N, Hoshiya H, Ragazzi M, Ferrari G, Kazuki Y, Moyle LA, Tonlorenzi R ... EMBO Molecular Medicine 10 (2), 254-275, 2018 | 36 | 2018 |
| Lentiviral Hematopoietic Stem Cell Gene Therapy Rescues Clinical Phenotypes in a Murine Model of Pompe Disease. G Piras, C Montiel-Equihua, YA Chan, S Wantuch, D Stuckey, D Burke, ... Mol Ther Methods Clin Dev, 558-570, 2020 | 14 | 2020 |
| Pericytes in muscular dystrophies LA Moyle, FS Tedesco, S Benedetti Biology of Pericytes: Development, Homeostasis and Disease, 319-344, 2019 | 14 | 2019 |
| Pre-clinical optimisation and safety studies of a new lentiviral gene therapy for p47phox-deficient chronic granulomatous disease A Schejtman, W Vetharoy, U Choi, C Rivat, N Theobald, G Piras, ... Human Gene Therapy, 2021 | 4 | 2021 |
| Targeting the central nervous system in lysosomal storage diseases: Strategies to deliver therapeutics across the blood-brain barrier BJ Critchley, HB Gaspar, S Benedetti Molecular Therapy, 00673-6, 2022 | 2 | 2022 |
| Gene and cell therapies for muscular dystrophies S Benedetti, G Cossu, FS Tedesco CRC Press, 2015 | 1 | 2015 |
