| Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells MD Hoban, GJ Cost, MC Mendel, Z Romero, ML Kaufman, AV Joglekar, ... Blood, The Journal of the American Society of Hematology 125 (17), 2597-2604, 2015 | 369 | 2015 |
| Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells MD Hoban, GJ Cost, MC Mendel, Z Romero, ML Kaufman, AV Joglekar, ... Blood, The Journal of the American Society of Hematology 125 (17), 2597-2604, 2015 | 369 | 2015 |
| CRISPR/Cas9-mediated correction of the sickle mutation in human CD34+ cells MD Hoban, D Lumaquin, CY Kuo, Z Romero, J Long, M Ho, CS Young, ... Molecular Therapy 24 (9), 1561-1569, 2016 | 227 | 2016 |
| High throughput sequencing analysis of RNA libraries reveals the influences of initial library and PCR methods on SELEX efficiency M Takahashi, X Wu, M Ho, P Chomchan, JJ Rossi, JC Burnett, J Zhou Scientific reports 6 (1), 1-14, 2016 | 102 | 2016 |
| AptaTRACE Elucidates RNA Sequence-Structure Motifs from Selection Trends in HT-SELEX Experiments P Dao, J Hoinka, M Takahashi, J Zhou, M Ho, Y Wang, F Costa, JJ Rossi, ... Cell Systems 3 (1), 62-70, 2016 | 70 | 2016 |
| Genetic regulation of OAS1 nonsense-mediated decay underlies association with COVID-19 hospitalization in patients of European and African ancestries AR Banday, ML Stanifer, O Florez-Vargas, OO Onabajo, BW Papenberg, ... Nature Genetics, 1-14, 2022 | 65 | 2022 |
| HSV-sr39TK positron emission tomography and suicide gene elimination of human hematopoietic stem cells and their progeny in humanized mice EH Gschweng, MN McCracken, ML Kaufman, M Ho, RP Hollis, X Wang, ... Cancer research 74 (18), 5173-5183, 2014 | 38 | 2014 |
| Dissecting the Mechanism of Histone Deacetylase Inhibitors to Enhance the Activity of Zinc Finger Nucleases Delivered by Integrase-Defective Lentiviral Vectors AV Joglekar, L Stein, M Ho, MD Hoban, RP Hollis, DB Kohn Human gene therapy 25 (7), 599-608, 2014 | 22 | 2014 |
| Anti-CD19 Chimeric Antigen Receptor Controlled By The Suicide Gene HSVsr39TK In Hematopoietic Stem Cells For Immunotherapy Of B-Lineage Malignancies SM Larson, A Tu, S Senadheera, M Ho, DB Kohn, S deOliveira Blood, The Journal of the American Society of Hematology 122 (21), 1659-1659, 2013 | 17 | 2013 |
| 338. Evaluation of TALENs and the CRISPR/Cas9 Nuclease System To Correct the Sickle Cell Disease Mutation MD Hoban, D Lumaquin, C Kuo, Z Romero, C Young, M Ho, J Long, ... Molecular Therapy 23, S135, 2015 | 3 | 2015 |
| Development of a CRISPR/Cas9 System for Mitochondrial Diseases M Ho, AH Pham, JJ Rossi, JC Burnett MOLECULAR THERAPY 28 (4), 39-40, 2020 | | 2020 |
| Site-Specific Correction of the Sickle Mutation in CD34+ Cells Using Zinc Finger Nucleases MD Hoban, AV Joglekar, D Gray, ML Kaufman, M Ho, Z Romero, ... MOLECULAR THERAPY 22, S291-S291, 2014 | | 2014 |
| Optimization and Characterization of Product Manufacturing for a Clinical Trial of Gene Therapy for Sickle Cell Disease F Urbinati, B Campo, J Wherley, S Geiger, ML Kaufman, AR Cooper, ... MOLECULAR THERAPY 22, S16-S16, 2014 | | 2014 |
| A Pre-Clinical Model Of Hematopoietic Stem Cell Based Immunotherapy For Cancer Utilizing The NY-ESO-1 T-Cell Receptor and sr39TK PET Reporter/Suicide Gene EH Gschweng, MN McCracken, T Chodon, RC Koya, ML Kaufman, M Ho, ... Blood, The Journal of the American Society of Hematology 122 (21), 2020-2020, 2013 | | 2013 |
| Enhancing the Efficiency of Zinc Finger Nuclease Delivery by Integrase-Defective Lentiviral Vectors Using Valproic Acid AV Joglekar, M Ho, L Stein, S Sanadiki, RP Hollis, DB Kohn MOLECULAR THERAPY 21, S190-S190, 2013 | | 2013 |
