| Efficient CRISPR/Cas9-mediated editing of trinucleotide repeat expansion in myotonic dystrophy patient-derived iPS and myogenic cells S Dastidar, S Ardui, K Singh, D Majumdar, N Nair, Y Fu, D Reyon, ... Nucleic acids research 46 (16), 8275-8298, 2018 | 89 | 2018 |
| Preclinical and clinical advances in transposon-based gene therapy J Tipanee, YC Chai, T VandenDriessche, MK Chuah Bioscience reports 37 (6), BSR20160614, 2017 | 84 | 2017 |
| Transposons: moving forward from preclinical studies to clinical trials K ChuahMarinee Human gene therapy, 2017 | 70 | 2017 |
| Next-generation muscle-directed gene therapy by in silico vector design S Sarcar, W Tulalamba, MY Rincon, J Tipanee, HQ Pham, H Evens, ... Nature communications 10 (1), 492, 2019 | 46 | 2019 |
| Universal allogeneic CAR T cells engineered with Sleeping Beauty transposons and CRISPR-CAS9 for cancer immunotherapy J Tipanee, E Samara-Kuko, T Gevaert, MK Chuah, T VandenDriessche Molecular Therapy 30 (10), 3155-3175, 2022 | 26 | 2022 |
| Meta-analysis of gene expression profiles identifies differential biomarkers for hepatocellular carcinoma and cholangiocarcinoma S Likhitrattanapisal, J Tipanee, T Janvilisri Tumor Biology 37, 12755-12766, 2016 | 17 | 2016 |
| Comprehensive transcriptome-wide analysis of spliceopathy correction of myotonic dystrophy using CRISPR-Cas9 in iPSCs-derived cardiomyocytes S Dastidar, D Majumdar, J Tipanee, K Singh, AF Klein, D Furling, ... Molecular Therapy 30 (1), 75-91, 2022 | 13 | 2022 |
| Validation of miR-20a as a tumor suppressor gene in liver carcinoma using hepatocyte-specific hyperactive piggyBac transposons J Tipanee, M Di Matteo, W Tulalamba, E Samara-Kuko, J Keirsse, ... Molecular Therapy-Nucleic Acids 19, 1309-1329, 2020 | 13 | 2020 |
| CRISPR/Cas9-mediated editing for dominant genetic disorders: efficient excision of trinucleotide repeat expansion in myotonic dystrophy S Dastidar, S Ardui, K Singh, N Nair, Y Fu, D Reyon, E Samara, MFM Gerli, ... Human Gene Therapy 28 (12), A7-A7, 2017 | 1 | 2017 |
| Hyperactive Transposons for cancer therapy J Tipanee | | 2020 |
| Validation of tumor suppressor microrna In liver tumorigenesis using hepatocyte-specific hyperactive piggybac transposons J Tipanee, M Di Matteo, W Tulalamba, E Samara-Kuko, J Keirsse, ... Human Gene Therapy 30 (11), A50-A50, 2019 | | 2019 |
| CRISPR/Cas9-Mediated Editing of Trinucleotide Repeat Expansion in Myotonic Dystrophy S Dastidar, K Singh, N Nair, Y Fu, D Reyon, E Samara, MFM Gerli, ... Molecular Therapy 25 (5), 85-85, 2017 | | 2017 |
| Next-generation muscle-directed gene therapy using skeletal-muscle specific transcriptional modules identified by genome-wide computational analysis S Sarcar, M Rincon, M Keyaerts, E Samara-Kuko, J Tipanee, ... Human Gene Therapy 26 (10), 2015 | | 2015 |
